Let’s build the next generation of RNA repair therapeutics

Many diseases are caused by mutations in genes that resist gene replacement or benefit from the safety features of our platform.

Many genes are too large to fit in a single AAV vector. Our platform supports the most efficient means to reconstitute full-length genes from dual AAV vectors

Apply engineered sequences to a chosen RNA, creating exquisitely cell type-specific expression of therapeutic proteins with applications in immuno-oncology.

Together, we can halt or reverse devastating illnesses that affect thousands of patients.